분자유전학실험실 (단국대학교 분자생물학과)



 이성욱 ( 2016-05-30 12:57:21 , Hit : 943
 GSK gets EU approval for first gene therapy for children

Life  |  Fri May 27, 2016 11:15am EDT


The GlaxoSmithKline building is pictured in Hounslow, west London, Britain, June 18, 2013.

Reuters/Luke MacGregor/File Photo

http://www.reuters.com/article/us-gsk-gene-therapy-idUSKCN0YI1VX

    

The world's first life-saving gene therapy for children, developed by GlaxoSmithKline and Italian scientists, was approved for sale in Europe on Friday, in a step forward for the pioneering technology to fix faulty genes.

Called Strimvelis, it is designed for a tiny number of children with ADA Severe Combined Immune Deficiency (ADA-SCID). SCID is sometimes known as “bubble baby” disease, since those born with it have immune systems so weak they must live in germ-free environments.

Strimvelis is the second gene therapy to be approved in Europe, after UniQure's Glybera, which treats a rare adult blood disorder.



ADVERTISING


inRead invented by Teads

Glybera made history in 2014 as the first drug to carry a $1 million price tag. GSK has not so far revealed how much its product will cost but a source close to the company said last month it would be “very significantly less than $1 million”.

The EU approval for GSK's treatment had been expected, following a positive opinion from the European Medicines Agency last month.

The U.S. Food and Drug Administration has yet to approve any gene therapies but a growing number of U.S. biotech companies have products in development.


(Reporting by Ben Hirschler; editing by Adrian Croft)







1147   DNA Can Be Edited Without Being Cut  이성욱 2016/08/30 1481
1146   Using RNA to Amplify RNA  이성욱 2016/08/16 1100
1145   CRISPR: No Cutting Required  이성욱 2016/08/06 1712
1144   “Kissing Disease” Virus Promotes Malignant Breast Cancer Development  이성욱 2016/08/03 1109
1143   Lytic and latent viral replication prevented with CRISPR/Cas9  이성욱 2016/07/27 979
1142   Chinese Scientists To Test Gene Modifying Technique ‘CRISPR’ On Humans For The First Time  이성욱 2016/07/27 1170
1141   FDA OKs AbbVie's once-daily Viekira XR for HCV-1  이성욱 2016/07/27 979
1140   [미국] 유전자가위 규제 마련 지연과 기업들의 움직임  이성욱 2016/07/21 1179
1139   5년새 20배 성장 `유전자치료제` 시장..경쟁력 확보 필수  이성욱 2016/07/21 1073
1138   Revisiting CAR T-Cells for Treating HIV Shows Promise  이성욱 2016/07/19 869
1137   코오롱, 유전자치료제 판매 허가 신청  이성욱 2016/07/12 979
1136   Gilead wins U.S. nod for drug for all types of hepatitis C  이성욱 2016/06/30 1034
1135   줄기세포·유전자치료제 차세대 주자로 급부상  이성욱 2016/06/21 1208
1134   Virus Hacks Host Genome, Steals CRISPR to Protect Itself  이성욱 2016/06/16 898
1133   CRISPR Antidotes Galore  이성욱 2016/06/14 1099
1132   Let’s Synthesize the Human Genome, Says HGP-Write  이성욱 2016/06/04 917
1131   A New CRISPR System for RNA  이성욱 2016/06/04 1013
1130   Scientists identify a novel CRISPR system that zeroes in on single-stranded RNA.  이성욱 2016/06/04 906
  GSK gets EU approval for first gene therapy for children  이성욱 2016/05/30 943
1128   Gene therapy drug approval granted to GSK  이성욱 2016/05/30 1006

[1][2][3][4][5][6] 7 [8][9][10]..[64] [다음 10개]
 

Copyright 1999-2023 Zeroboard / skin by ROBIN